Seeking boys between the ages of 6 and 12 with Duchenne Muscular Dystrophy (DMD) who can walk for a study of the effectiveness and safety of an investigational drug.
We are studying whether an investigational drug given in combination with systemic corticosteroids is more effective than a placebo (looks like the drug but contains no medication) given in combination with systemic corticosteroids in improving muscle strength and heart and lung function. Participants will get an infusion of the drug or placebo every 2 weeks for a year.
What we're hoping for
We hope to evaluate whether the investigational drug is more effective than placebo in improving muscle strength and heart and lung function in boys ages 6-12 who have Duchenne Muscular Dystrophy.
ClinicalTrials.gov Identifier: NCT04632940