Seeking people aged 6 and older who are taking Givinostat for Duchenne Muscular Dystrophy (DMD) for an observational study looking at the experience of patients with DMD who are taking givinostat.
Seeking boys aged 8-12 with no history of fragility fractures and boys aged 12-16 with a history of fragility fractures for a study of an investigational drug to prevent muscle and bone weakness due to Duchene Muscular Dystrophy
Seeking boys aged 1 to less than 12 years old who have Duchenne muscular dystrophy for a study of an investigational gene therapy to cause muscle cells to produce microdystrophin.
Seeking boys aged 2 and older with Duchenne Muscular Dystrophy who have been prescribed Vamorolone (Agamree) for a study of the long-term safety of the drug.
Seeking boys aged 4 to 16 for a study of an investigational drug to increase dystrophin protein levels in muscles.
Seeking boys and men with Duchenne muscular dystrophy (DMD) or Becker Muscular Dystrophy (BMD) to provide samples including blood, plasma, serum, urine, as well as the remainders of tissue samples collected as part of their usual clinical care for a biorepository.
Seeking male participants aged 10-21 years of age who have been diagnosed with Duchenne Muscular Dystrophy (DMD) for participation in an imaging study.
This study is intended to collect data from medical records on patients who have Duchenne Muscular Dystrophy