Study Of An Investigational Drug For Duchenne Muscular Dystrophy
Seeking boys aged 7, 8, or 9 who have Duchenne Muscular Dystrophy and are ambulatory for a study of an investigational drug.
9 Studies found
Bone Joint and Muscle Diseases
Bone Joint and Muscle Diseases
Study Of Duchenne Muscular Dystrophy Patients Taking Givinostat
Seeking people aged 6 and older who are taking Givinostat for Duchenne Muscular Dystrophy (DMD) for an observational study looking at the experience of patients with DMD who are taking givinostat.
Bone Joint and Muscle Diseases
Study Of An Investigational Drug For Duchene Muscular Dystrophy
Seeking boys aged 8-12 with no history of fragility fractures and boys aged 12-16 with a history of fragility fractures for a study of an investigational drug to prevent muscle and bone weakness due to Duchene Muscular Dystrophy
Bone Joint and Muscle Diseases
Study Of An Investigational Gene Therapy For Duchenne Muscular Dystrophy
Seeking boys aged 1 to less than 12 years old who have Duchenne muscular dystrophy for a study of an investigational gene therapy to cause muscle cells to produce microdystrophin.
Bone Joint and Muscle Diseases
Study Of The Long-Term Safety Of Vamorolone In Patients With Duchenne Muscular Dystrophy
Seeking boys aged 2 and older with Duchenne Muscular Dystrophy who have been prescribed Vamorolone (Agamree) for a study of the long-term safety of the drug.
Bone Joint and Muscle Diseases
Study Of An Investigational Drug To Preserve Muscle Function In Boys With Duchenne Muscular Dystrophy
Seeking boys aged 4 to 16 for a study of an investigational drug to increase dystrophin protein levels in muscles.
Bone Joint and Muscle Diseases
Duchenne Muscular Dystrophy (Dmd) And Becker Muscular Dystrophy (Bmd) Biorepository
Seeking boys and men with Duchenne muscular dystrophy (DMD) or Becker Muscular Dystrophy (BMD) to provide samples including blood, plasma, serum, urine, as well as the remainders of tissue samples collected as part of their usual clinical care for a biorepository.
Bone Joint and Muscle Diseases
Imaging Study Of Individuals Diagnosed With Duchenne Muscular Dystrophy (Dmd)
Seeking male participants aged 10-21 years of age who have been diagnosed with Duchenne Muscular Dystrophy (DMD) for participation in an imaging study.
Bone Joint and Muscle Diseases
Data Collection Study For Patients With Duchenne Muscular Dystrophy
This study is intended to collect data from medical records on patients who have Duchenne Muscular Dystrophy