Study Of An Investigational Drug For Duchenne Muscular Dystrophy
Seeking boys aged 7, 8, or 9 who have Duchenne Muscular Dystrophy and are ambulatory for a study of an investigational drug.
Seeking boys aged 7, 8, or 9 who have Duchenne Muscular Dystrophy and are ambulatory for a study of an investigational drug.
Seeking people aged 6 and older who are taking Givinostat for Duchenne Muscular Dystrophy (DMD) for an observational study looking at the experience of patients with DMD who are taking givinostat.
Seeking boys aged 2 and older with Duchenne Muscular Dystrophy who have been prescribed Vamorolone (Agamree) for a study of the long-term safety of the drug.
Seeking people diagnosed with Chronic Fatigue Syndrome, Long COVID, Chronic Lyme, Fibromyalgia, Gulf-War Illness, Hypermobile EDS or Hypermobility Syndrome, Postural orthostatic tachycardia syndrome (POTS),or Orthostatic Intolerance for a study collecting blood, urine, saliva and skin tissue.
Seeking adults aged 18 and older who either have Facioscapulohumeral Muscular Dystrophy (FSHD) or are healthy volunteers for a study to identify genetic biomarkers for the disease and better understand what causes it, and why symptoms vary widely among people who have it.
Seeking boys and men with Duchenne muscular dystrophy (DMD) or Becker Muscular Dystrophy (BMD) to provide samples including blood, plasma, serum, urine, as well as the remainders of tissue samples collected as part of their usual clinical care for a biorepository.
Seeking male participants aged 10-21 years of age who have been diagnosed with Duchenne Muscular Dystrophy (DMD) for participation in an imaging study.
This study is intended to collect data from medical records on patients who have Duchenne Muscular Dystrophy
Seeking adults who have had low back pain for at least 3 months for a study of whether things such as activity levels, sleep, heart rate, or emotions impact how their pain responds to mindfulness treatment.
Seeking men and women whose rheumatoid arthritis has not responded to TNF-biologic treatment for a study comparing two different types of treatments (non-TNFi-biologic and tsDMARDs).
Seeking adults who have inflammatory arthritis and who are willing to provide data by answering questionnaires, giving a blood sample and donating leftover tissue samples for a study to help researchers better understand inflammatory arthritis.
This is a registry to collect medical record information from people living with Multiple Sclerosis (MS) to better understand the disease and develop new treatments